Sunday, April 8, 2018

Strong correlations among four measures of disease progression in Friedreich's ataxia

Harry J. Saal PhD, Frederic Heerinckx, Rezi Zawadzki DrPH, Omid Omidvar MD, Marcus Kilpatrick PhD, Theresa Zesiewicz MD, Movement Disorders : Official Journal of the Movement Disorder Society [06 Apr 2018] Letter DOI: 10.1002/mds.27351

Using the data from a double-blind, placebo-controlled trial in 19 FRDA patients testing RT001 a linoleic acid derivative, baseline FARS-Neuro scores were compared with T25FW and CPET to measure peak workload/kg and peak oxygen consumption.

  Strong correlations among four measures of disease progression in Friedreich's ataxia